Winners of the National Draw 2016


National Draw emblem

Winners of the National Draw 2016

Thank you to everyone who bought and sold tickets for the National Draw. The money you raised from the draw will provide support for individuals and families affected by MPS and related diseases as well as funding research into treatments and

The SMC decision regarding Migalastat (Galafold)

The SMC decision regarding Migalastat (Galafold) was announced on 07 November 2016.  The relevant Detailed Advice Document can be found here.

Christine Lavery to receive 2017 patient Advocate Leader Award

WORLDSymposium™ announces Christine Lavery, MBE, Group Chief Executive for the Society for Mucopolysaccharide Diseases, as the recipient for the 2017 Patient Advocate Leader (PAL) Award. Please go to for the full announcement.

Migalastat for treating Fabry disease

The MPS Society is pleased to announce that NICE has given an interim recommendation for Migalastat to be used as a treatment option for Fabry disease in patients over the age of 16 years. This is not the final recommendation

Bupa Home Healthcare now owned by Celesio

Celesio, a leading healthcare services company, announced in July the completion of its agreement with Bupa to purchase Bupa Home Healthcare, a clinical home healthcare provider. This follows Competition and Market Authority (CMA) approval on 28th June. The addition of