Take to the Skies for MPS Awareness Day!


Take to the Skies for MPS Awareness Day!

We are delighted to have teamed up with Shire, the National MPS Society and the International MPS Network to bring you a brand new campaign to mark MPS Awareness Day! Take to the Skies and Fly for MPS this year

Thank you!

Thank you to everyone who helped us to mark MPS Awareness Day on 15th May 2016! Whether you Wore It Blue, Took to the Skies, held a party, bake sale or raffle, you all did a great job of raising

Approval for Galafold™ in patients with Fabry announced

Amicus Therapeutics, a biotechnology company at the forefront of rare and orphan diseases, today announced that the European Commission has granted full approval for the oral small molecule pharmacological chaperone Galafold™ (migalastat) as a first line therapy for long-term treatment