We encourage you to send in questions for the speakers. Please add your question when registering for this event.

Agenda:

• Welcome and housekeeping rules - Sophie Thomas, Senior Head of Patient Services and Clinical Liaisons, MPS Society
• Overview of therapy options for MPS I – James Davison - UK
• Small Activating RNA post-transplant in MPS I -  Dr Simon Jones - UK
• Lentiviral Gene Therapy for MPS I – Professor Maria Ester Bernardo - Italy
• Invivo Gene therapy – Dr Raymond Wang – USA
• Encapsulated Allogeneic MPS I Therapy – Dr Thomas Kenny - UK
• IV therapy – Professor Roberto Giugliani - Brazil
• Summary and closing comments - Sophie Thomas, Senior Head of Patient Services and Clinical Liaisons, MPS Society