Thu, 17 Jun | Zoom

MPS I Clinical trial and treatment update webinar

Join us for our first MPS I webinar specifically on new treatments. The webinar is for patients, families, carers, and professionals interested in learning more about upcoming treatments and clinical trials.
Registration is Closed
MPS I Clinical trial and treatment update webinar

Time & Location

17 Jun, 19:00 – 20:20
Zoom

About the Event

We encourage you to send in questions for the speakers. Please add your question when registering for this event.

Agenda:

  • Welcome and housekeeping rules - Sophie Thomas, Senior Head of Patient Services and Clinical Liaisons, MPS Society
  • Overview of therapy options for MPS I – James Davison - UK
  • Small Activating RNA post-transplant in MPS I -  Dr Simon Jones - UK
  • Lentiviral Gene Therapy for MPS I – Professor Maria Ester Bernardo - Italy
  • Invivo Gene therapy – Dr Raymond Wang – USA
  • Encapsulated Allogeneic MPS I Therapy – Dr Thomas Kenny - UK
  • IV therapy – Professor Roberto Giugliani - Brazil
  • Summary and closing comments - Sophie Thomas, Senior Head of Patient Services and Clinical Liaisons, MPS Society
Registration is Closed