GM1 Gangliosidosis

What is GM1 Gangliosidosis?


GM1 gangliosidosis is an inherited lysosomal storage disease that progressively destroys nerve cells (neurons) in the brain and spinal cord.


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Contact us


Our support line is open 9-5pm

Monday-Friday: 0345 389 9901

Out of hours line: open 5pm-10pm Monday-Friday and weekends:

07712 653 258