This webinar for Fabry patients and their families provides information about available interventional studies, who is eligible for them and how to make contact with centres.
Speakers and subjects included:
ERT clinical studies – Derralynn Hughes
Oral monotherapy studies – Ana Jovanovic
Arrhythmia study in Fabry patients – Ravi Vijapurapu
In vivo gene therapy – Derralynn Hughes
Investigational gene therapy – Tarek Hiwot
Summary of Fabry treatments, studies and trials
At the webinar, we promised you a document providing information on new treatments and details of the ongoing research studies and clinical trials underway in the UK for Fabry. We are pleased to share this summary which was prepared by Rare Disease Research Partners for MPS Society and we hope you find it useful.
Watch the full webinar
The webinar was recorded live and is available to view below.
Find more support, information and resources to help you with social distancing and coronavirus if you are living with MPS, Fabry or a related disease at our dedicated COVID-19 pages. Or you can follow our weekly Wednesday webinars series here.
If you have found this information helpful please consider donating to the MPS Society.