Gene therapy for MPS

The American Society of Gene & Cell Therapy (ASGCT) have developed a series of patient-friendly resources to educate on gene therapy approaches for MPS. Visit their website to find more information about gene therapy for MPS and to see more videos and resources on the subject. Here's a their gene therapy basics video to give you an idea of what to expect.


Gene therapy basics


Gene therapy has been studied for more than 40 years and can help stop or slow the effects of disease on the most basic level of the human body - our genes. And to understand how it works, we’ll start at the basics.


We are the only registered charity providing professional support to individuals and families affected by MPS, Fabry or a related disease in the UK.

Sign up for our monthly newsletter below

MPS Society

MPS House, Repton Place

White Lion Road, Amersham

Buckinghamshire, HP7 9LP

  • Twitter - White Circle
  • Facebook - White Circle

Registered Charity No.1143472 & SCO41012. Registered Company No. 7726882.

Images and stories may not be reproduced without express written permission. 

© 2019 Society for Mucopolysaccharide Diseases