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Video published on 15 November 2019

Gene Therapy for MPS by Derralynn Hughes

MPS National Conference 2019 Gene Therapy for MPS by Derralynn Hughes Lysosomal Storage Disorders Unit, Royal Free London NHS Foundation Trust, University College London

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My Fabry treatment: a guide to empower and inform Fabry patients on their treatment journey

Sam just does "normal stuff"

Contact us

Make a difference

My Fabry treatment: a guide to empower and inform Fabry patients on their treatment journey

Sam just does "normal stuff"

Contact us

Make a difference

Gene Therapy for MPS by Derralynn Hughes

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Consent

My Fabry treatment: a guide to empower and inform Fabry patients on their treatment journey

Sam just does "normal stuff"

Contact us

Make a difference

My Fabry treatment: a guide to empower and inform Fabry patients on their treatment journey

Sam just does "normal stuff"

Contact us

Make a difference

More videos

Fabry disease - Neurology update by Mark Roberts

Fabry Disease - What to look for in children by Anupam Chakrapani

Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

Family tree and the role of the genetic counsellors in metabolic MDT clinics by Dr Karolina Stepien

Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

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