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Treatments and research

Through medical research and clinical trials, we know we will find innovative ways in which to cope with living with MPS, Fabry or a related lysosomal disease.
The MPS Society shares knowledge, expertise and works in partnership and collaboration with other patient organisations, medical authorities and scientific institutions across the world, in order to facilitate progress towards research and better treatment for those living with one of our conditions.
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Current treatments for MPS, Fabry and related diseases consist largely of Enzyme Replacement Technology and Hematopoietic Stem Cell Transplantation.

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Clinical trials

Parents and patients are encouraged to talk to their expert clinician to discuss whether there are any clinical trial opportunities. 

Contact the support and advocacy team

Our helpline is open 9-5pm Monday-Friday: 0345 389 9901 or you can email:
Out of hours support line: open 5pm-10pm Monday-Friday and weekends: 07712 653 258 

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